Outcomes in Patients With Leber Hereditary Optic Neuropathy Treated With Intravitreal rAAV2/2- ND4

This secondary analysis of data from a phase 1/2 clinical trial examines the association between immune response and intraocular inflammation after ocular gene therapy with recombinant adeno-associated virus 2 carrying the ND4 gene in patients with Leber hereditary optic neuropathy.

source https://jamanetwork.com/journals/jamaophthalmology/fullarticle/2723597